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"path": "/news/2026-06-gene-therapy-life-threatening-inherited.html",
"publishedAt": "2026-06-17T15:00:06.000Z",
"site": "https://medicalxpress.com",
"textContent": "A new gene therapy appears to be safe in patients diagnosed with Friedreich ataxia cardiomyopathy, a progressive and fatal inherited cardiac disease, according to a phase 1 clinical trial led by Weill Cornell Medicine researchers. The treatment may also reduce heart damage, although further investigation is needed.",
"title": "Gene therapy shows promise for life-threatening inherited heart disease"
}