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"path": "/news/2026-03-fda-gene-therapy-severe-leukocyte.html",
"publishedAt": "2026-03-28T11:30:02.000Z",
"site": "https://medicalxpress.com",
"textContent": "Dr. Donald Kohn has been developing gene therapies for rare pediatric immune disorders for over 30 years. This week, his role in a clinical trial has culminated in the first-ever U.S. Food and Drug Administration–approved therapy for severe leukocyte adhesion deficiency-I—a genetic condition characterized by recurrent infections and, often, early death.",
"title": "FDA approves gene therapy for severe leukocyte adhesion deficiency-I, a rare immune disorder"
}